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*Public Policy Tipoffs Involving Maryland Newsletter for 2024-12-22 ( 3 items )  
Cystic Fibrosis Foundation: FDA Approves Trikafta for 94 Additional Rare CFTR Mutations (10)
BETHESDA, Maryland, Dec. 21 -- Cystic Fibrosis Foundation issued the following news release on Dec. 20, 2024: * * * The U.S. Food and Drug Administration (FDA) today approved the expansion of Trikafta (elexacaftor/tezacaftor/ivacaftor) to people with cystic fibrosis ages 2 and older who have at least one of 94 rare mutations in the cystic fibrosis transmembrane conductance regulator (CFTR) gene. * * * The approval enables a small number of people with cystic fibrosis in the U.S. who were not more PR

Foundation Fighting Blindness: ViGeneron Receives FDA Authorization to Launch Clinical Trial for MRNA Trans-Splicing Gene Therapy for Stargardt Disease (10)
COLUMBIA, Maryland, Dec. 21 -- The Foundation Fighting Blindness issued the following news: * * * The company is also planning to conduct the clinical trial at sites in the EU. * * * ViGeneron, a company developing genetic therapies for eye diseases, has received authorization from the US Food & Drug Administration (FDA) to launch a Phase 1/2 clinical trial for VG801, an emerging mRNA trans-splicing gene therapy for people with Stargardt disease and other retinal diseases caused by mutations more PR

Virginia Tech recognizes graduates at 2024 fall commencement (10)
BLACKSBURG, Virginia, Dec. 20 -- Virginia Tech issued the following news: Commencement events on Friday honored students who completed their academic degrees during the summer and fall terms. Margie Lee '82, DVM '86, who transformed poultry health research and broke barriers in veterinary medicine and is now associate dean for research and graduate studies at the Virginia-Maryland College of Veterinary Medicine, delivered the keynote address at the university ceremony. Two graduate students El more PR